First gene therapy provision for DMD in Abu Dhabi by Department of Health, Abu Dhabi

The Department of Health – Abu Dhabi (DoH), the regulator of the healthcare sector, has provided revolutionary gene therapy for Duchenne Muscular Dystrophy (DMD) for the first time in Abu Dhabi and outside the United States.

While previously the therapy was accessible only in the United States, this groundbreaking treatment will now also be offered at Sheikh Khalifa Medical City (SKMC), part of SEHA; a subsidiary of PureHealth, further cementing Abu Dhabi's position as a leading healthcare destination and life sciences hub globally.

DMD is a hereditary neuromuscular disorder that causes the muscles to gradually weaken over time. Through this treatment, DoH and the SKMC medical team used Delandistrogene moxeparvovec; a one-time injection that has proven to be effective in addressing the underlying cause of DMD. The treatment can potentially transform the disease trajectory by delivering functional dystrophin genes into patient cells which help the body produce biologically active dystrophin protein for muscle function, improving muscle strength and the patient's quality of life. Following the FDA's announcement of expanding the Delandistrogene moxeparvovec treatment to children four and above, DoH remains committed to providing comprehensive care and support to affected patients and their families.

H.E. Dr. Noura Khamis Al Ghaithi, Undersecretary of Department of Health – Abu Dhabi (DoH), said: "This medical milestone underscores Abu Dhabi's continuous dedication to adopting world-class healthcare innovations that create a distinguished and holistic healthcare experience to all members of the community and beyond. We are committed to continuing to bring advanced preventative, diagnostics and therapeutic capabilities to the region, reinforcing Abu Dhabi's position as a leading healthcare and medical tourism destination".